Hydrolytic Lysosomal Glycogen-specific Enzyme [EPC] class drugs

2 results
  • lumizyme - alglucosidase alfa injection, powder, for solution

    (Alglucosidase Alfa)
    Genzyme Corporation
    Lumizyme is indicated for patients with Pompe disease (acid alpha-glucosidase deficiency), a rare genetic condition affecting lysosomal glycogen breakdown.
  • nexviazyme - avalglucosidase alfa - ngpt injection, powder, lyophilized, for solution

    (Avalglucosidase Alfa-Ngpt)
    Genzyme Corporation
    Nexviazyme treats late-onset Pompe disease (lysosomal acid alpha-glucosidase deficiency) in patients 1 year and older.