Phenylalanine Hydroxylase Activator class drugs

1 result
  • kuvan

    (SAPROPTERIN DIHYDROCHLORIDE)
    BioMarin Pharmaceutical Inc.
    KUVAN® is indicated for reducing blood phenylalanine levels in patients aged one month and older with hyperphenylalaninemia due to tetrahydrobiopterin-responsive Phenylketonuria, to be used alongside a phenylalanine-restricted diet.