Transthyretin-directed RNA Interaction class drugs

3 results
  • amvuttra

    (VUTRISIRAN)
    Alnylam Pharmaceuticals, Inc.
    AMVUTTRA is indicated for treating the polyneuropathy associated with hereditary transthyretin-mediated amyloidosis in adults.
  • onpattro

    (patisiran)
    Alnylam Pharmaceuticals, Inc.
    ONPATTRO is indicated for treating the polyneuropathy associated with hereditary transthyretin-mediated amyloidosis in adults.