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  • Medications for Fabry Disease

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    3 results
    • elfabrio

      (pegunigalsidase alfa)
      Chiesi USA, Inc.
      Usage: ELFABRIO is indicated for the treatment of adults with confirmed Fabry disease.
    • fabrazyme

      (AGALSIDASE BETA)
      Genzyme Corporation
      Usage: FABRAZYME® is indicated for the treatment of adult and pediatric patients aged 2 years and older who have confirmed Fabry disease.
    • galafold

      (migalastat hydrochloride)
      Amicus Therapeutics US, LLC
      Usage: GALAFOLD is indicated for treating adults with a confirmed diagnosis of Fabry disease and an amenable GLA gene variant. The indication is based on accelerated approval following a reduction in kidney interstitial capillary cell globotriaosylceramide (KIC GL-3) substrate. Continued approval may require further clinical benefit verification.